9th Annual Gene Therapy Symposium for Heart, Lung, and Blood Diseases
Focus Topic: Gene Expression
November 17-19, 2010 - Sonoma, California

Program

Wednesday, November 17, 2010 - Welcoming Reception

Thursday, November 18, 2010

Keynote Speaker

• Andrew M. Scharenberg, M.D. (University of Washington)
  “Strategies for Enhancing Site Specific Genome Engineering Efficiency”

Session I  

• Brian D. Brown, Ph.D. (Mt Sinai Medical Center)
  “Utilizing Synthetic microRNA Sites for Targeting Vector Expression”

• David V. Schaffer, Ph.D. (University of California, Berkeley)
  “Directed Evolution of New Viruses with Novel Gene Delivery Properties”

• Michele P. Calos, Ph.D. (Stanford University)
  “Triple Recombinase Strategy to Make and Modify Induced Pluripotent Stem Cells”

Session II   

• W. Robb MacLellan, M.D. (UC Los Angeles)
  “Human Cardiovascular Progenitor Cells, Induced Pluripotent Stem Cells and Epigenetic Regulation of Cardiac Fate”
  

• Ian McNiece, Ph.D. (University of Miami)
  “Mesenchymal Stem Cells and Ischemic Heart Repair”

• Ian MacLachlan, Ph.D. (Tekmira Pharmaceuticals)
  “Integrating Preclinical and Clinical Experience in the Development of the Next Generation of siRNA Products”

“Practical Strategies”: Evaluating the Safety of RNAi-based Therapeutics

• Beverly L. Davidson, Ph.D. (University of Iowa)

Jacuzzi Family Vineyards

Workshop: “Biomaterials and Tissue Engineering”

• Lonnie D. Shea, Ph.D. (Northwestern University)

Session III

• Mark A. Krasnow, M.D., Ph.D. (Stanford University)
  “Progenitor and Stem Cells in Lung Development and Disease”

• Angela Panoskaltsis-Mortari, Ph.D. (University of Minnesota)
  “Bioengineering of the Lung using iPS Cells and Decellularized Lung Matrix”
  
  
• Barry J. Byrne, M.D., Ph.D. (University of Florida)
  "Phase 2 Trial of rAAV1-hAAT"

Session IV

• R. Keith Humphries, M.D., Ph.D. (University of British Columbia)
  “Targeting the Untargetable: Leukemogenic Transcription Factors”
  
  
• Mary C. Dinauer, M.D., Ph.D. (Washington University)
  “Antibody Targeting c-Kit as a Pre-Transplant Conditioning for Gene Therapy”
  
  
• Eirini P. Papapetrou, M.D., Ph.D. (Memorial Sloan Kettering)
  “Genetic Engineering of Patient-Specific Induced Pluripotent Stem Cells in Genomic 'Safe Harbors'”