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11th Annual Gene Therapy Symposium for Heart, Lung, and Blood Diseases
Focus Topic: Translation and Clinical Trials
November 14-16, 2012 - Sonoma, California
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Wednesday, November 14, 2012 - Welcoming Reception
Thursday, November 15, 2012
Keynote Speaker
- Luigi Naldini, M.D., Ph.D. (San Raffaele Telethon Institute for Gene Therapy)
“Genetic Engineering of Human Hematopoiesis for Treating Inherited Diseases and Cancer”
Session I: Vectors
- Kenneth G. Cornetta, M.D. (Indiana University)
“The Destiny of Lentiviral Vectors - Research Oddity or FDA Approved Treatment?"”
- David Schaffer, Ph.D. (UC Berkeley)
“Directed Evolution of New Viruses for Therapeutic Gene Delivery”
- Bruce Sullenger, Ph.D. (Duke University)
“Driving Innovation by Forward and Reverse Translation of Aptamers”
Student/Fellow Presentations and Poster Session - Link to Information
Session II
- John P. Cooke, M.D., Ph.D. (Stanford University)
“Nuclear Programming to Pluripotency Requires Activation of Innate Immunity Pathways: An Overlooked Effect of Viral Vectors Leads to New Reprogramming Approach”
- Emerson C. Perin, M.D. Ph.D. (Texas Heart Institute)
“Translational Issues for Cardiovascular Stem Cell Trials: Focus on Delivery”
- Roger J. Hajjar, M.D. (Mount Sinai School of Medicine)
“Gene Therapy for the Treatment of Heart Failure”
“Practical Strategies”: Endothelial Progenitors
- Mervin C. Yoder, M.D. (Indiana University)
Dinner at the Markham Winery |
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Friday, November 16, 2012
Workshop: “Translation to Clinical Trials”
Student/Fellow Presentations and Poster Session - Link to Information
Session III
- Paula M. Cannon, Ph.D. (University of Southern California)
“Pre-Clinical Evaluation of Anti-HIV Gene Therapies in Humanized Mice”
- Donald B. Kohn, M.D. (University of California, Los Angeles)
“Gene Therapy Using Hematopoietic Stem Cells”
- Barry J. Byrne, M.D., Ph.D. (University of Florida)
"Treatment Strategies for Pompe Disease: Lessons from Preclinical and Clinical Studies"
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