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10th Annual Gene Therapy Symposium for Heart, Lung, and Blood Diseases
Focus Topic: Cell Trafficking and the Niche
November 16-18, 2011 - Sonoma, California
Student/Fellow Presentations |
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Thursday, November 17, 2011
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Janet Chung, Ph.D.
(City of Hope)
“Multiplexing Small Nucleolar RNAs to Inhibit HIV-1 Replication”
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Tania I. Fuentes, B.S.
(Loma Linda University)
“Co-transplantation of Mesenchymal Stem Cells and Human Stem Cell-Derived Cardiomyocytes for Cardiovascular Repair Activates Host-Derived Cardiovascular Progenitor Cells” |
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Megan D. Hoban, B.S.
(University of California, Los Angeles)
“Efficient and Transient Delivery of Zinc Finger Nucleases by Non-Integrating Lentiviral Vectors” |
Ulrike Jung, Ph.D.
(City of Hope)
“Addition of a Modified polyA Signal and Intron into a Lentiviral Platform for RNAi and Protein Over-Expression Provides Potent Efficacy while Maintaining High Vector Titers”
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Christina A. Pacak, Ph.D.
(Harvard University)
“Characterization of a Muscle Derived Stem Cell to Develop a Bioengineered Alternative to Pacemakers for Children with AV Block” |
Nutan Prasain, Ph.D.
(Indiana University)
“miR302 Cluster Completes iPS Cell Reprogramming through Suppression of MBD2”
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Barbara K. Smith, Ph.D., P.T.
(University of Florida)
“Phase I/II Trial of Diaphragm Gene Therapy for Pompe Disease: Initial Ventilatory Outcomes” |
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Friday, November 18, 2011
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Denise Carbonaro, Ph.D.
(Stanford University)
“Factor VIII Gene Therapy”
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David D. Dickey, B.S.
(University of Iowa)
“Directed Evolution of AAV in Pig Airway Epithelia In Vivo” |
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Sabine Geiger, M.S.
(University of California, Los Angeles)
“Preclinical Studies for Gene Therapy of Sickle Cell Disease using Bone Marrow CD34+ Cells modified with a ßAS3-Globin Lentiviral Vector”
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Katrin Hacke, Ph.D.
(University of California, Los Angeles)
“Combined Preconditioning and In Vivo Chemoselection with 6-Thioguanine Alone Results in Highly Efficient Reconstitution of Normal Hematopoiesis with HPRT-Deficient Bone Marrow” |
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Sushrusha Nayak, Ph.D.
(University of Florida)
“Successful Rituximab Based Immune Modulation for Pompe Disease”
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Benjamin R. Steines, B S.
(University of Iowa)
“AAV2 and AAV8 as Gene Therapy Vectors Targeting Distal Lung Epithelial Progenitor Cells” |
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Heather L. Thompson, B.S.
(University of California, Merced)
“Host F4/80+ Splenic Macrophages are Increased after Transplantation of Allogeneic Embryonic Stem Cell-Derived Hematopoietic Progenitors”
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